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Number of items:
1
.
Author:
Ms Tabea Stock
Supervisor:
Prof. Dr. Bernd Wilken, Dr. Gudrun Schreiber
Group:
Neuropaediatrics
Keywords:
spinal muscular atrophy (sma)
,
nusinersen (spinraza)
,
quality of life (qol)
,
muscle function
,
treatment
Nusinersen: A new treatment option for spinal muscular atrophy. Efficacy and outcome measurement
Research Project Report (2018-2019)
This list was generated on
Sat May 21 23:42:42 2022 BST
.