Nusinersen: A new treatment option for spinal muscular atrophy. Efficacy and outcome measurement
Research Project Report (2018-2019)
| Author: | Ms Tabea Stock |
|---|---|
| Supervisor: | Prof. Dr. Bernd Wilken, Dr. Gudrun Schreiber |
| Group: | Neuropaediatrics |
| Keywords: | spinal muscular atrophy (sma), nusinersen (spinraza), quality of life (qol), muscle function, treatment |